Gene therapy education materials for the sickle cell disease community

Overview

Presently, there are only a handful of options to manage or treat sickle cell disease.  

Now, researchers are developing new and emerging gene therapies to treat sickle cell disease.

To help navigate these new therapies, more than 50 scientists, physicians, patients and other experts worked together to develop content for the Democratizing Education for Sickle Cell Disease Gene Therapy Project, which is led by NHGRI in partnership with other organizations and individuals. This group met over the course of four workshops.